The multiyear research program will evaluate a novel approach to improve the function of the defective
In people with cystic fibrosis, mutations in the CF
If successful, the potential messenger RNA therapy could benefit all people with cystic fibrosis, regardless of an individual's mutations.
“The Cystic Fibrosis Foundation is pursuing many exciting research avenues to speed the development of new treatments for all people with cystic fibrosis,” said Robert J. Beall, Ph.D., president and CEO of the Cystic Fibrosis Foundation. “Shire brings a promising new approach and significant research capabilities to our efforts to find a cure for this devastating disease.”
The first phase of Shire's CF research program is focused on evaluating the
The Foundation has built a robust pipeline of potential therapies that target cystic fibrosis from every angle. Currently, the Foundation has research initiatives with leading biotechnology and pharmaceutical companies such as Pfizer, Genzyme and Vertex to discover and develop drugs to treat the basic genetic defect in CF.